臨床眼科78巻11号

2024年10月発行

増刊号 6年前の常識は現在の非常識！—AI時代へ向かう今日の眼科医へ

Ⅷ．網膜

遺伝子治療

著者： 池田康博¹

所属機関： ¹宮崎大学医学部感覚運動医学講座眼科学分野

ページ範囲：P.220 - P.226

文献概要

ここが変わった！

以前の常識

・遺伝子治療は次世代の治療と考えられていた．

・保険適用になるとは考えられていなかった．

・対象となる疾患は，遺伝性網膜ジストロフィのような難治性疾患と考えられていた．

現在の常識

・RPE65関連網膜症に対する遺伝子治療が保険適用となった．

・加齢黄斑変性や糖尿病黄斑浮腫に対する治験も実施されている．

・遺伝子治療が標準治療として認められるようになりつつある．

参考文献

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